Families of SMA committed new funding to the following SMA research projects during 2012:
-$710,000 for Basic Research.
-$1,450,000 for Drug Discovery.
-$110,000 for Clinical Trial Resources.
-$200,000 for the 16th SMA Research Group Meeting.
Funding was provided to the following institutions:
There are now have 3 clinical trials testing new SMA therapies, and an additional 10 programs in earlier stages of the drug development pipeline. The FSMA research approach funds programs at early stages, and then partners with companies to take them through clinical trials. Supporting multiple programs gives different approaches for a SMA therapy, which increases the chances of success and accelerates the timeline to a treatment and cure.
Families of SMA will announce more funding in the New Year, which will include 3 more new drug programs to add to the pipeline. In addition, the organization will launch a brand new effort for funding of patient care research in order to improve the standard of care.
About Families of SMA
Families of Spinal Muscular Atrophy (FSMA) is the world’s leader focused on funding SMA research to develop a treatment and cure for the disease. The successful results and progress that the organization has delivered, from basic research to drug discovery to clinical trials, provide real hope for families and patients impacted by the disease. The charity has invested over $55 million in research and has been involved in funding half of all the ongoing novel drug programs for SMA.
Families of SMA is a nonprofit 501(c)3 organization, with 31 Chapters and 90,000 members and supporters throughout the United States. The organization’